Adrenoleukodystrophy research

The Future of Adrenoleukodystrophy

The future of ALD lies in research in gene expression and other experimental models of the disease to again further insights into the disease. Research on gene expression and using animal models might help us to understand why some ALD positive patients go on to develop the disease and some do not, but there are moral questions to ask. As for all genetical specifications, the hypothesis of gene therapy has been debated, but doubts stay on over how such therapy could be carried out. Screening during birth would distinguish those at danger from ALD but there are moral queries over whether it could it be rationalised, especially as medication is not at nowadays ensured. Family analyses could also distinguish those at danger, but questions persist over how far such reports ought to be granted. Heterozygotes, those who bear the ALD gene, could be cared in the time to come and adults with AMN, the adult form of ALD should also be considered.